Cell and Gene Therapy

This course introduces and explores the principles, theory and concepts that underpin cell and gene therapy. This rapidly advancing area in bioscience is recognised as having the potential to revolutionise therapy for inherited disorders and many other diseases.

The course starts by examining the implications of the human genome project and reviews the function of DNA, chromosomes, RNA transcription and translation. It then considers the significance of Recombinant DNA techniques, and the use of mRNA and vector design in effective gene therapy. The course also considers the impact of cell therapy and the characteristics and significance of stem cells and the issues and challenges faced in transplantation and integration, alongside ethical and regulatory concerns.